Clinical Perspective: Treating RPE65-Associated Retinal Dystrophy
Journal: 2020/December - Molecular Therapy
Abstract:
Until recently, there was no treatment for inherited retinal blindness. Late in 2017, LuxturnaTM became the first approved gene therapy product for a genetic disease in the USA and in the European Union, changing the situation. This article presents current considerations regarding the administration of this treatment in the clinic.
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